CRISPR-based gene editing therapy approved by the FDA for the first time
December 8, 2023TS & G bloggerComments Off on CRISPR-based gene editing therapy approved by the FDA for the first time
In a landmark decision, the FDA greenlit two new drugs for the treatment of sickle cell disease in patients 12 and older, one of which —Vertex’s drug Casgevy — is the first approved use of genome editing technology CRISPR in the US. Bluebird Bio’s Lyfgenia also is a cell-based gene…